- Rare condition drug ‘fundamentally changed’ boy’s life BBC
- NHS drugs go-ahead offers lifeline to children with rare muscle-wasting disease The Guardian
- NHS to roll out ‘life-changing’ spinal muscular atrophy treatments for children Sky News
- ‘Life-changing’ SMA treatments to be made routinely available on NHS The Independent
- Pop star backs calls for screening after twins diagnosed with genetic disorder Oxford Mail
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